Agamree, an approved steroid treatment for Duchenne MD, will be sold in Turkey by GEN, per an agreement with Santhera.

A protein called MYOD has long been known to be able to turn on genes, but a recent study has found that it also can turn off ...

Enrollment is now ongoing in a first-in-human clinical trial testing EPI-321, a therapy designed to target the underlying ...

Columnist Shalom Lin and his partner, Amanda — both disabled artists — find that their challenges are exactly what can drive ...

The FDA has granted breakthrough therapy designation to DYNE-251 for the treatment of DMD in patients amenable to exon 51 ...

In both good times and bad, the importance of human connection cannot be understated, columnist Patrick Moeschen writes.

View this post on Instagram Day 13 of 30 Days of MD Topic: Advocating for Disability Through My Blog and Video Podcast This is @cognizantclay’s story: Hello everyone! My name is Clayton Theriault. I ...

View this post on Instagram Day 8 of 30 Days of MD Topic: Poem About MD This is @writingpoemsinthedark’s story: Simply put, I write to connect. Poetry allows me to address and work through topics that ...

View this post on Instagram Day 23 of 30 Days of MD Topic: Being a Dad with Becker's MD This is @dystrophydad ’s story: I was diagnosed with Becker’s Muscular Dystrophy at birth. I remember the day my ...

Columnist Robin Stemple, his brothers, and more enjoy a long-in-the works family music celebration at his mother's nursing home.