Agamree, an approved steroid treatment for Duchenne MD, will be sold in Turkey by GEN, per an agreement with Santhera.

Columnist Robin Stemple, his brothers, and more enjoy a long-in-the works family music celebration at his mother's nursing home.

A protein called MYOD has long been known to be able to turn on genes, but a recent study has found that it also can turn off ...

In both good times and bad, the importance of human connection cannot be understated, columnist Patrick Moeschen writes.

Enrollment is now ongoing in a first-in-human clinical trial testing EPI-321, a therapy designed to target the underlying ...

Columnist Shalom Lin and his partner, Amanda — both disabled artists — find that their challenges are exactly what can drive ...

The FDA has granted breakthrough therapy designation to DYNE-251 for the treatment of DMD in patients amenable to exon 51 ...

Columnist Betty Vertin, whose days often feel overloaded, describes how it feels when her life as a caregiver is recognized and affirmed.

Columnist Shalom Lim is energized by a recent program for youth leaders in Singapore that matched them with people from the MD community.

What if the risk vs. reward choice focused on your medical care or treatment options? How do you weigh risk vs. reward if your life is at stake, and how do you weigh your own morals, ethics, and ...